US AI in Drug Discovery Market - Forecasts From 2025 To 2030

Report CodeKSI061618230
PublishedDec, 2025

Description

United States AI in Drug Discovery market is anticipated to expand at a high CAGR over the forecast period.

US AI In Drug Discovery Market Key Highlights:

  • Cost Imperative: The cost of developing a new drug creates a massive financial catalyst, driving demand for AI platforms that can significantly reduce preclinical failure rates and cycle times.
  • Oncology Leadership: The Oncology segment accounted for the largest therapeutic area revenue share in 2022, reflecting intensive adoption of AI for identifying targeted therapeutics and novel biomarkers for complex cancers.
  • Evolving Regulatory Framework: The FDA's active engagement, evidenced by the release of draft guidance on the use of AI in regulatory decision-making, signals increasing regulatory maturity, which validates and propels industry-wide adoption.

The integration of Artificial Intelligence (AI) into the US drug discovery pipeline represents a fundamental transformation of the biopharmaceutical research and development (R&D) paradigm. Historically constrained by the enormous capital requirements and the high-risk, high-failure nature of conventional processes, the industry now leverages AI to navigate the vast chemical and biological space with unprecedented speed and precision. The core value proposition of AI, specifically Machine Learning (ML) and Deep Learning, is the ability to rapidly process petabytes of complex genomic, proteomic, and clinical data to identify novel drug targets, predict compound toxicity, and optimize lead molecules. This shift is not merely an enhancement of existing workflows but an essential strategic imperative for large pharmaceutical companies, which must accelerate their pipeline replenishment and improve R&D return on investment to sustain competitive advantage in a complex therapeutic landscape. The US remains the epicenter of this market, characterized by significant venture capital funding, a robust academic research ecosystem, and the direct engagement of major regulatory bodies like the FDA.

US AI In Drug Discovery Market Analysis:

  • Growth Drivers

The escalating cost and time associated with bringing a novel therapeutic to market directly propels demand for AI solutions. AI platforms directly address this by recognizing hit and lead compounds, providing quicker validation of the drug target, and reducing the drug discovery timeline. The increasing prevalence of chronic diseases globally imposes a considerable economic burden on health services, generating immense pressure on pharmaceutical companies to accelerate the development of new, effective treatments. This urgency creates immediate, high-priority demand for AI tools that offer better predictive modeling and higher success rates in early-stage research.

  • Challenges and Opportunities

A significant market constraint is the persistent scarcity of high-quality, normalized, and proprietary biological and chemical datasets essential for training robust and unbiased AI models. Furthermore, the lack of transparency or explainability (XAI) in certain Deep Learning models creates a barrier, as regulatory bodies require a verifiable rationale for compound selection, thereby tempering demand for black-box solutions. Conversely, a major opportunity lies in the expanding use of AI in clinical trial optimization, specifically in patient stratification and protocol design, which is driven by the industry's need to reduce the high cost and failure rate of clinical phases. The increasing availability of real-world data (RWD) and Electronic Health Records (EHR) also creates immediate demand for AI platforms that can aggregate and analyze this massive data to validate targets and predict patient outcomes.

  • Supply Chain Analysis

The US AI in Drug Discovery market’s supply chain is a value chain composed of intangible assets and specialized services, centered on data, algorithms, and computational infrastructure. The chain begins with Data Generation and Curation (Pharmaceutical/Biotech companies, CROs, and academic institutes), which is the most critical dependency, as model efficacy hinges on data quality and scale. This data is processed by AI/ML Platform Providers (Software developers, cloud providers like NVIDIA/AWS), representing the central processing hub where algorithms are trained on high-performance computing (HPC) systems. The end-users, Pharmaceutical and Biotechnology Companies consume the predictive models and insights. Logistical complexity is not physical but Computational and Regulatory, revolving around data security, intellectual property rights for proprietary algorithms, and the significant expense of securing the necessary high-end computing chips and cloud infrastructure.

US AI In Drug Discovery Market Government Regulations

The US regulatory environment is evolving rapidly to accommodate AI, influencing market demand through compliance requirements and incentives for innovation.

Jurisdiction

Key Regulation / Agency

Market Impact Analysis

United States

FDA Draft Guidance: AI to Support Regulatory Decision-Making for Drug and Biological Products

This guidance, released in early 2025, requires a risk framework based on the 'context of use' of the AI model. This directly creates demand for specialized AI governance, validation tools, and Explainable AI (XAI) capabilities to ensure compliance and transparency in regulatory submissions.

United States

FDA CDER AI Council (Established 2024)

The establishment of the Center for Drug Evaluation and Research (CDER) AI Council coordinates the agency's response to AI use across the drug life cycle. This institutionalizes AI adoption, signaling regulatory stability and increasing demand for consistent, high-quality data science practices within pharmaceutical submissions.

United States

ICH Q9(R1) Quality Risk Management

Updated guidance that emphasizes quality risk management aligns with AI's capability in predictive quality control and continuous improvement during manufacturing. This promotes the integration of AI-based Process Analytical Technology (PAT) solutions, driving demand in the later-stage development segment.

US AI In Drug Discovery Market Segment Analysis:

  • By Technology: Deep Learning

The Deep Learning technology segment commands high demand because it surpasses traditional Machine Learning in its capacity to process and extract non-linear, complex feature relationships from vast, multi-dimensional biological datasets, such as high-content cellular images, transcriptomics, and complex genomic sequences. Unlike older computational methods, deep learning, particularly Convolutional Neural Networks (CNNs) and Generative Adversarial Networks (GANs), can automate feature engineering, accelerating the identification of subtle patterns indicative of a druggable target or a toxic compound. The demand for Deep Learning is specifically driven by its utility in Generative AI for de novo molecule design, allowing researchers to explore novel chemical spaces and generate new compounds with optimized properties, fundamentally increasing the speed and creativity of the Hit-to-Lead and Lead Optimization phases. This technological advantage is a strategic imperative for biopharma companies seeking genuine first-in-class therapies.

  • By Application: Lead Optimization

The Lead Optimization application segment exhibits robust demand because it is the phase where small-molecule candidates are fine-tuned for critical properties like ADMET (Absorption, Distribution, Metabolism, Excretion, and Toxicity). This stage is computationally intensive and highly prone to failure. AI platforms, specifically those utilizing Deep Learning on proprietary data, drastically improve the predictive accuracy of compound properties in silico before expensive wet-lab testing. The demand for AI in this segment is driven by the industry's critical need to reduce the high attrition rate of compounds that fail due to poor pharmacokinetics or toxicity, which are estimated to account for up to 50% of late-stage failures. By applying predictive AI, pharmaceutical end-users can significantly lower the overall R&D cost and time by eliminating unsuitable candidates earlier, directly leading to a high willingness to invest in these predictive tools.

US AI In Drug Discovery Market Competitive Environment and Analysis:

The competitive environment is a highly dynamic ecosystem defined by technological capability and strategic partnerships. The landscape features a mix of pure-play TechBio firms (like Recursion and Exscientia) that treat biology as an information science, and legacy Big Pharma companies that integrate AI through M&A or high-value collaborations. Competitive advantage is derived from the size and quality of proprietary biological datasets and the demonstrable ability to move AI-discovered candidates rapidly into the clinic.

  • Company Profile: Recursion Pharmaceuticals

Recursion Pharmaceuticals is strategically positioned as a leading clinical-stage TechBio company, fundamentally integrating robotics, computer vision, and machine learning into a unified platform they term the Recursion Operating System (OS). The core of their strategy is to generate one of the largest proprietary, high-dimensional biological and chemical datasets in the world, spanning over 65 petabytes. In May 2024, the company announced the completion of BioHive-2, an NVIDIA DGX SuperPOD AI supercomputer, which results in four times faster speeds than their original supercomputer. This significant capacity addition solidifies their strategic positioning by enabling the training of larger, more generalized foundation models and AI agents to industrialize the entire drug discovery effort.

  • Company Profile: Insilico Medicine

Insilico Medicine operates as a clinical-stage biotechnology company that utilizes generative AI platforms for target discovery and de novo molecule design. The company's strategic positioning is predicated on demonstrating the end-to-end capability of its platform, Pharma.AI, to deliver novel candidates from discovery to IND-enabling studies in accelerated timelines. A critical competitive advantage is their demonstration of regulatory success.

US AI In Drug Discovery Market Developments:

  • November 20, 2024: Recursion and Exscientia Combination

Recursion Pharmaceuticals and Exscientia plc officially combined to advance the industrialization of drug discovery, an event that followed the August 8, 2024, definitive agreement announcement. This merger represents a major consolidation in the TechBio space, combining two leading AI platforms to create a global technology-enabled drug discovery leader with end-to-end capabilities, effectively raising the capital and technological bar for competitors.

  • May 13, 2024: Recursion Completes NVIDIA-Powered BioHive-2

Recursion announced the completion of BioHive-2, their new NVIDIA DGX SuperPOD AI supercomputer, powered by 63 DGX H100 systems. This capacity addition, which results in four times faster speeds than the previous system, constitutes the largest supercomputer in the pharmaceutical industry and provides the computational muscle necessary to train larger and more generalizable foundation models for accelerating drug discovery.

  • July 10, 2024: Exscientia Launches AWS AI-powered Platform

Exscientia plc announced the launch of its expanded AWS AI-powered platform to further accelerate drug discovery. This expansion integrated AWS's AI/ML services beyond the DesignStudio to include the robotic automation of synthesis and testing in their AutomationStudio. This development highlights a continuous product launch cycle focused on integrating generative AI drug design with automated lab operations to deliver molecular candidates faster and more cost-effectively.

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United States AI in Drug Discovery Market Segmentation:

  • BY OFFERING
    • Software
    • Services
  • BY TECHNOLOGY
    • Machine Learning
    • Deep Learning
    • Natural Language Processing (NLP)
    • Other AI Technologies
  • BY THERAPEUTIC AREA
    • Oncology
    • Neurology
    • Cardiovascular Diseases
    • Infectious Diseases
    • Others
  • BY APPLICATION
    • Target Identification and Validation
    • Hit-to-Lead Identification
    • Lead Optimization
    • Drug Repurposing
    • Others
  • BY END-USERS
    • Pharmaceutical Companies
    • Biotechnology Companies
    • Contract Research Organizations (CROs)
    • Research Institutes
    • Others

Table Of Contents

1. EXECUTIVE SUMMARY

2. MARKET SNAPSHOT

2.1. Market Overview

2.2. Market Definition

2.3. Scope of the Study

2.4. Market Segmentation

3. BUSINESS LANDSCAPE

3.1. Market Drivers

3.2. Market Restraints

3.3. Market Opportunities

3.4. Porter’s Five Forces Analysis

3.5. Industry Value Chain Analysis

3.6. Policies and Regulations

3.7. Strategic Recommendations

4. TECHNOLOGICAL OUTLOOK

5. UNITED STATES AI IN DRUG DISCOVERY MARKET BY OFFERING

5.1. Introduction

5.2. Software

5.3. Services

6. UNITED STATES AI IN DRUG DISCOVERY MARKET BY TECHNOLOGY

6.1. Introduction

6.2. Machine Learning

6.3. Deep Learning

6.4. Natural Language Processing (NLP)

6.5. Other AI Technologies

7. UNITED STATES AI IN DRUG DISCOVERY MARKET BY THERAPEUTIC AREA

7.1. Introduction

7.2. Oncology

7.3. Neurology

7.4. Cardiovascular Diseases

7.5. Infectious Diseases

7.6. Others

8. UNITED STATES AI IN DRUG DISCOVERY MARKET BY APPLICATION

8.1. Introduction

8.2. Target Identification and Validation

8.3. Hit-to-Lead Identification

8.4. Lead Optimization

8.5. Drug Repurposing

8.6. Others

9. UNITED STATES AI IN DRUG DISCOVERY MARKET BY END-USERS

9.1. Introduction

9.2. Pharmaceutical Companies

9.3. Biotechnology Companies

9.4. Contract Research Organizations (CROs)

9.5. Research Institutes

9.6. Others

10. COMPETITIVE ENVIRONMENT AND ANALYSIS

10.1. Major Players and Strategy Analysis

10.2. Market Share Analysis

10.3. Mergers, Acquisitions, Agreements, and Collaborations

10.4. Competitive Dashboard

11. COMPANY PROFILES

11.1. IBM Corporation

11.2. Microsoft Corporation

11.3. Alphabet Inc. (Google)

11.4. NVIDIA Corporation

11.5. Atomwise, Inc.

11.6. BenevolentAI

11.7. Exscientia Ltd.

11.8. Insilico Medicine

11.9. Cyclica Inc.

11.10. Cloud Pharmaceuticals, Inc.

12. APPENDIX

12.1. Currency

12.2. Assumptions

12.3. Base and Forecast Years Timeline

12.4. Key benefits for the stakeholders

12.5. Research Methodology

12.6. Abbreviations

LIST OF FIGURES

LIST OF TABLES

Companies Profiled

IBM Corporation

Microsoft Corporation

Alphabet Inc. (Google)

NVIDIA Corporation

Atomwise, Inc.

BenevolentAI

Exscientia Ltd.

Insilico Medicine

Cyclica Inc.

Cloud Pharmaceuticals, Inc.

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