The gaucher disease treatment market is estimated to be valued at US$1,673.076 million and is projected to grow at a healthy rate during the forecast period. Gaucher’s disease is a genetic disease leading to fatty substances (sphingolipids) accumulation in cells and certain organs. The disease is caused by a hereditary deficiency of the enzyme beta-glucocerebrosidase (GCase). In the case of the defective enzyme, glucosylceramide can collect in the spleen, liver, kidneys, lungs, brain, and bone marrow. The severity of Gaucher disease varies, but it is ultimately fatal. The growing demand for rare disease treatment is one of the major factors driving the growth of the global gaucher disease treatment market. Treatment for the Type 1 Gaucher is available, but for the other stages, type 2 and type 3, there is at present no cure. Technological advancements and rising R&D investments will promote the development of new drugs creating an opportunity for the growth of the gaucher disease treatment market in the forecast period and beyond. Gaucher disease is more common among Jews of Ashkenazi (Eastern European) descent, occurring in approximately 1 in 450 within this population (National Gaucher Foundation). Europe is expected to hold a significant market share owing to the disease prevalence in this region.
This research study examines the current market trends related to the demand, supply, and sales, in addition to the recent developments. Major drivers, restraints, and opportunities have been covered to provide an exhaustive picture of the market. The analysis presents in-depth information regarding the development, trends, and industry policies and regulations implemented in each of the geographical regions. Further, the overall regulatory framework of the market has been exhaustively covered to offer stakeholders a better understanding of the key factors affecting the overall market environment.
Identification of key industry players in the industry and their revenue contribution to the overall business or relevant segment aligned to the study have been covered as a part of competitive intelligence done through extensive secondary research. Various studies and data published by industry associations, analyst reports, investor presentations, press releases and journals among others have been taken into consideration while conducting the secondary research. Both bottom-up and top down approaches have been utilized to determine the market size of the overall market and key segments. The values obtained are correlated with the primary inputs of the key stakeholders in the gaucher disease treatment value chain. The last step involves complete market engineering which includes analyzing the data from different sources and existing proprietary datasets while using various data triangulation methods for market breakdown and forecasting.
Market intelligence is presented in the form of analysis, charts, and graphics to help the clients in gaining faster and efficient understanding of the gaucher disease treatment market.
Major industry players profiled as part of the report are Sanofi Genzyme, Shire Plc (Takeda Pharmaceutical Company Limited), Pfizer Inc., and ORPHAZYME A/S among others.
The gaucher disease treatment market has been analyzed through following segments: